Stem cell trial a first for pediatric traumatic brain injury


February 3, 2011

In conjunction with Children’s Memorial Hermann Hospital, the Medical School has begun enrollment for the first Phase I safety study approved by the Food and Drug Administration to investigate the use of a child’s own umbilical cord blood stem cells for traumatic brain injury in children.

The innovative study is led by principal investigator Dr. Charles Cox, the Children’s Fund Distinguished Professor of Pediatric Surgery and Pediatrics, and director of the pediatric trauma program at Children’s Memorial Hermann Hospital. It will enroll 10 children ages 18 months to 17 years who have umbilical cord blood banked with Cord Blood Registry (CBR) and have suffered moderate to severe traumatic brain injury. The study is not designed for acute care and will only enroll participants within 6–18 months of the injury.

Although the neurologic outcome for nearly all types of brain injury (with the exception of abuse) is better for children than adults, trauma is the leading cause of death in children, and the majority of the deaths are attributed to head injury.

“Using cord blood is a critical link in the next step of UTHealth’s programmatic approach to researching stem cell therapies for brain injury,” Cox said. “Implementing this novel therapy has required strong partnerships with Children’s Memorial Hermann Hospital and the CBR Center for Regenerative Medicine and is possible through a critical infrastructure investment by the state of Texas and private philanthropy.”

To enroll in the study, parents or caregivers of patients who have suffered a traumatic brain injury should contact CBR, and after consent is obtained, the information will be relayed to the UTHealth research group. If all qualifications are met, the patient will travel to Children’s Memorial Hermann Hospital, where the cells will be processed and intravenously infused. Patients will be followed at six months, one year, and two years.

A recently completed Phase I study at UTHealth (publication in press), which investigated a bone-marrow stem cell therapy in children with acute traumatic brain injury, revealed positive safety results, Cox said.

The FDA-authorized protocol is specific to the standardized processing and storage protocol of CBR, making it the only family stem cell bank providing patients for the study.

“This study is at the forefront of research evaluating a child’s own cord blood stem cells’ ability to help facilitate the healing process after damage to nerve tissue in the brain,” said Heather Brown, vice president of scientific and medical affairs at Cord Blood Registry. “CBR is helping advance medical research for regenerative therapies by connecting the child whose family banked with CBR to appropriate researchers.”

— Deborah Mann Lake, Office of Advancement, Media Relations